Our Promise To Patients

You've likely had a long journey, but now you're among friends. We understand rare and serious conditions because we've specialized in it for decades and we're here to help. By working closely with people like Omar (pictured above), we're able to identify and pursue new innovations that address unmet medical needs. Meanwhile, we continue to enhance our current treatments for conditions, including immunodeficiency and autoimmune diseases, and other bleeding disorders.

We are driven by our promise to save lives and improve the quality of life for our patients and their families, because living with a rare disease impacts more than just one person. We offer support programs and activities and we partner with patient advocacy organizations to improve and expand educational and outreach efforts. We also work with government authorities to ensure patients have access to the medicines they need to live life to the fullest.